Severe combined immune deficiency (SCID) patients lack a functional immune system, making them incredibly vulnerable to infection. In the past the only way to keep these children safe was to keep them in plastic chambers, to protect them from the risk of infection.
The team at St Jude Children’s Research Hospital have pioneered a new treatment for these children; gene therapy. By replacing the defective gene with a copy that works correctly the team at St Jude were able to observe an immune response within the 10 patients involved in this trial within three months.
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